Leukodystrophy - 153 Studies Found
Enrolling by invitation |
: Long-term Follow-up of Subjects With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product :
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Completed |
: Exercise Study of Function and Pathology for Women With X-linked Adrenoleukodystrophy : X-linked Adrenoleukodystrophy : 2012-05-07 : Behavioral: exercise training The exercise program uses a local Curves® gym to provide an individua |
Recruiting |
: Observational Study to Evaluate Allogeneic HSCT Outcomes for Cerebral Adrenoleukodystrophy (CALD) :
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Not yet recruiting |
: Early Diagnosis Of Childhood Cerebral ALD : Adrenoleukodystrophy : 2016-10-25 |
Recruiting |
: Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy :
: 2015-08-12 : Genetic: transduced CD34+ hematopoietic stem cell Autologous hematopoietic stem cells (HSCs) collected f |
Active, not recruiting |
: MD1003-AMN MD1003 in Adrenomyeloneuropathy : : 2024-05-14 |
Completed |
: A Clinical Trial for AMN: Validation of Biomarkers of Oxidative Stress, Efficacy and Safety of a Mixture of Antioxidants : Adrenomyeloneuropathy : 2011-11-28 :
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Terminated |
: Study of Bile Acids in Patients With Peroxisomal Disorders :
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Completed |
: Compassionate Treatment of Patients With Inborn Errors of Bile Acid Metabolism With Cholic Acid :
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